A Phase III Study to Determine the Role of Ixazomib as an Augmented Conditioning Therapy in Salvage Autologous Stem Cell Transplant (ASCT) and as a Post-ASCT Consolidation and Maintenance Strategy in Patients With Relapsed Multiple Myeloma

Who is this study for? Patients with Multiple Myeloma
What treatments are being studied? Ixazomib+Thalidomide+Dexamethasone+Conventional Autologous Stem Cell Transplant+ITD Consolidation+Ixazomib
Status: Recruiting
Location: See all (91) locations...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 3
SUMMARY

Study design: Randomised, controlled, multi-centre, open-label, phase III trial (with a single intervention registration phase). Primary Objectives The primary objectives of this study are to determine: * The impact on Depth of Response (DoR: less than VGPR versus VGPR or better) when salvage ASCT conditioning is augmented by the addition of a proteasome inhibitor * The influence of a consolidation and maintenance strategy on the Durability of Response (DuR:PFS) Secondary objectives The secondary objectives of this study are to determine: * Overall survival * Time to disease progression * The overall response rate following ixazomib, thalidomide and dexamethasone (ITD) re-induction * Time to next treatment * Progression-free survival 2 (PFS2) * Duration of response * Minimal Residual Disease (MRD) negative rate post re-induction, post-ASCT and conversion after ITD consolidation * Engraftment kinetics * Toxicity and safety * Quality of life (QoL) Participant population (refer to protocol section 9 for a full list of eligibility criteria). * Relapsed MM (with measurable disease by IMWG criteria) previously treated with ASCT * First progressive disease (PD) at least 12 months since first ASCT, requiring therapy. * ECOG Performance Status 0-2 * Aged at least 18 years * Adequate full blood count and renal, hepatobiliary, pulmonary and cardiac function * Written informed consent Interventions: All participants will be registered at trial entry and will receive re-induction therapy with 4-6, 28-day cycles of ixazomib, thalidomide and dexamethasone (ITD), in order to reach maximum response. Participants who achieve at least stable disease (SD) will be randomised on a 1:1 basis to receive either conventional ASCT (ASCTCon), using melphalan, or augmented ASCT (ASCTAug), using melphalan with ixazomib. All participants achieving or maintaining a minimal response (MR) or better following trial ASCT will undergo a second randomisation to consolidation and maintenance or no further treatment. Participants randomised to consolidation and maintenance will receive treatment as follows: consolidation with 2 cycles of ITD and maintenance with ixazomib until disease progression. Number of participants: 406 participants will be registered into the trial to allow 284 participants to be randomised at the first randomisation (R1) and 248 participants to be randomised at the second randomisation (R2).

Eligibility
Participation Requirements
Sex: All
Minimum Age: 18
Healthy Volunteers: f
View:

• Diagnosed with relapsed MM (with measurable disease, according to IMWG criteria (Appendix 2)) previously treated with ASCT).

• First Progressive Disease (PD) at least 12 months following first ASCT, requiring therapy.

• Eastern Cooperative Oncology Group (ECOG) Performance Status 0-2 (Appendix 3).

• Aged at least 18 years.

• Participants must have the following blood results within 14 days before registration:

∙ Absolute neutrophil count (ANC) ≥1x109/L

‣ Platelet count ≥75x109/L. If the participant has ≥50% bone marrow infiltration a platelet count of ≥50x109/L is allowed.

• Platelet transfusions are not allowed within 3 days before registration in order to meet these values.

• Adequate renal function within 14 days before registration:

• a. Creatinine clearance ≥30ml/min (calculated according to the Cockcroft-Gault equation or other locally approved formula)

• Adequate hepatobiliary function within 14 days before registration:

∙ Total bilirubin \<2 x upper limit of normal (ULN)

‣ ALT \<2 x ULN

• Adequate pulmonary function within 14 days before registration:

• a. Adequate respiratory functional reserve (delineated by KCO/DLCO (carbon monoxide diffusion in the lung) of ≥50%). No evidence of a history of pulmonary disease. If a significant history, then a review by a respiratory medicine physician is required.

• Adequate cardiac function within 12 weeks before registration

• a. Left ventricular ejection fraction (LVEF) ≥40%. Note: repeat confirmation of cardiac function is needed if treatment is given between this assessment and registration.

⁃ Female participants who:

• Are not of childbearing potential (Appendix 8), OR

∙ If they are of childbearing potential (Appendix 8), agree to practice 2 effective methods of contraception (Appendix 8), at the same time, from the time of signing the informed consent form until 90 days after the last dose of study drug, OR

∙ Agree to practice true abstinence when this is in line with the preferred and usual lifestyle of the subject. (Periodic abstinence \[e.g. calendar, ovulation, symptothermal, post-ovulation methods\] and withdrawal are not acceptable methods of contraception.)

⁃ Male participants, even if surgically sterilised (i.e. status post-vasectomy), must agree to one of the following:

∙ Agree to practice effective barrier contraception during the entire study treatment period and through 90 days after the last dose of study drug, OR

∙ Agree to practice true abstinence when this is in line with the preferred and usual lifestyle of the subject. (Periodic abstinence (e.g. calendar, ovulation, symptothermal, post-ovulation methods\] and withdrawal are not acceptable methods of contraception.) Contraception for female and male participants must be in accordance with (and consent to) the Celgene-approved Thalidomide Pregnancy Prevention Programme.

⁃ If female and of childbearing potential (see Appendix 8), must have a negative pregnancy test performed by a healthcare professional in accordance with the Celgene Thalidomide Pregnancy Prevention Programme.

⁃ Patients agree not to receive other clinical trials treatment, including investigational medicinal products (IMPs) not included in this trial, within 30 days of trial registration and throughout the duration of the trial, until disease progression.

⁃ Able to provide written informed consent.

Locations
Other Locations
United Kingdom
Aberdeen Royal Infirmary
RECRUITING
Aberdeen
Monklands Hospital
RECRUITING
Airdrie
University Hospital Ayr
RECRUITING
Ayr
Barnsley Hospital
RECRUITING
Barnsley
Basingstoke & North Hampshire Hospital
RECRUITING
Basingstoke
Royal United Hospital
RECRUITING
Bath
Good Hope Hospital
RECRUITING
Birmingham
Heartlands Hospital
RECRUITING
Birmingham
Queen Elizabeth Hospital
RECRUITING
Birmingham
Blackpool Victoria Hospital
RECRUITING
Blackpool
Pilgrim Hospital
RECRUITING
Boston
Royal Bournemouth Hospital
RECRUITING
Bournemouth
Bradford Royal Infirmary
RECRUITING
Bradford
Bristol Haematology & Oncology Centre
RECRUITING
Bristol
Southmead Hospital
RECRUITING
Bristol
Queen's Hospital
RECRUITING
Burton Upon Trent
Addenbrooke's Hospital
RECRUITING
Cambridge
St Helier Hospital
RECRUITING
Carshalton
Cheltenham General Hospial
RECRUITING
Cheltenham
Countess of Chester Hospital
RECRUITING
Chester
Chesterfield Royal Hospital
RECRUITING
Chesterfield
St Richards Hospital
RECRUITING
Chichester
University Hospital Coventry
RECRUITING
Coventry
Royal Derby Hospital
RECRUITING
Derby
Dewsbury Hospital
RECRUITING
Dewsbury
Russells Hall Hospital
RECRUITING
Dudley
Ninewells Hospital
RECRUITING
Dundee
Hairmyres Hospital
RECRUITING
East Kilbride
Western General Hospital
RECRUITING
Edinburgh
Beatson Cancer Centre
RECRUITING
Glasgow
New Victoria Hospital
RECRUITING
Glasgow
Gloucestershire Royal Hospital
RECRUITING
Gloucester
Grantham and District Hospital
RECRUITING
Grantham
Diana Princess of Wales Hospital
RECRUITING
Grimsby
Calderdale Royal Hospital
RECRUITING
Halifax
Harrogate District Hospital
RECRUITING
Harrogate
Huddersfield Royal Infirmary
RECRUITING
Huddersfield
Castle Hill Hospital
RECRUITING
Hull
Raigmore Hospital
RECRUITING
Inverness
Ipswich Hospital
RECRUITING
Ipswich
Kidderminster Hospital
RECRUITING
Kidderminster
University Hospital Crosshouse
RECRUITING
Kilmarnock
St James's University Hospital
RECRUITING
Leeds
Leicester Royal Infirmary
RECRUITING
Leicester
Lincoln County Hospital
RECRUITING
Lincoln
Royal Liverpool University Hospital
RECRUITING
Liverpool
University Hospital Aintree
RECRUITING
Liverpool
Guys and St Thomas's Hospital
RECRUITING
London
Kings College Hospital
RECRUITING
London
Royal Marsden Hospital
RECRUITING
London
St Barts Hospital
RECRUITING
London
University College London Hospital
RECRUITING
London
Maidstone Hospital
RECRUITING
Maidstone
Manchester Royal Infirmary
RECRUITING
Manchester
The Christie
RECRUITING
Manchester
Borders General Hospital
RECRUITING
Melrose
James Cook University Hospital
RECRUITING
Middlesbrough
Milton Keynes General Hospital
RECRUITING
Milton Keynes
Freeman Hospital
RECRUITING
Newcastle
North Tyneside General Hospital
RECRUITING
North Shields
Norfolk & Norwich University Hospital
RECRUITING
Norwich
Nottingham City Hospital
RECRUITING
Nottingham
Royal Oldham Hospital
RECRUITING
Oldham
Churchill Hospital
RECRUITING
Oxford
Royal Alexandra Hospital
RECRUITING
Paisley
Derriford Hospital
RECRUITING
Plymouth
Pontefract Hospital
RECRUITING
Pontefract
Whiston Hospital
RECRUITING
Prescot
Royal Berkshire Hospital
RECRUITING
Reading
Redditch Hospital
RECRUITING
Redditch
Salford Royal Hospital
RECRUITING
Salford
Salisbury Hospital
RECRUITING
Salisbury
Scunthorpe General Hospital
RECRUITING
Scunthorpe
Royal Hallamshire Hospital
RECRUITING
Sheffield
Southampton General Hospital
RECRUITING
Southampton
St Helens Hospital
RECRUITING
St Helens
Stafford County Hospital
RECRUITING
Stafford
Stepping Hill Hospital
RECRUITING
Stockport
Royal Stoke University Hospital
RECRUITING
Stoke-on-trent
Sunderland Royal Hospital
NOT_YET_RECRUITING
Sunderland
King's Mill Hospital
RECRUITING
Sutton In Ashfield
Singleton Hospital
RECRUITING
Swansea
Musgrove Park Hospital
RECRUITING
Taunton
St George's Hospital
RECRUITING
Tooting
Tunbridge Wells Hospital
RECRUITING
Tunbridge Wells
Pinderfields General Hospital
RECRUITING
Wakefield
Royal Hampshire County Hospital
RECRUITING
Winchester
Wishaw Hospital
RECRUITING
Wishaw
New Cross Hospital
RECRUITING
Wolverhampton
Worcestershire Royal Hospital
RECRUITING
Worcester
Worthing Hospital
RECRUITING
Worthing
Contact Information
Primary
Gwen Jacques, Senior Trial Coordinator
ctru-myelomaxii@leeds.ac.uk
0044 113 343 1159
Backup
Trial Management Assistant
ctru-myelomaxii@leeds.ac.uk
0044 113 343 5476
Time Frame
Start Date: 2017-03-20
Estimated Completion Date: 2027-03
Participants
Target number of participants: 406
Treatments
Active_comparator: Conventional Autologous Stem Cell Transplant (ASCT)
Melphalan 200mg/m2 IV infusion on Day -1, followed by ASCT on Day 0
Experimental: Augmented Autologous Stem Cell Transplant (ASCT)
Melphalan 100mg/m2 IV infusion on Day -3 and -2 plus ixazomib 4mg capsules on Day -4 and -1. ASCT will then be given on Day 0.
Sponsors
Collaborators: Cancer Research UK, Takeda
Leads: University of Leeds

This content was sourced from clinicaltrials.gov