Safety and Impact on Quality of Life of Focused Ultrasound Pallidotomy for Dyskinetic Cerebral Palsy in Pediatric and Young Adult Subjects

Status: Recruiting
Location: See location...
Intervention Type: Device
Study Type: Interventional
Study Phase: Not Applicable
SUMMARY

The primary objective of the proposed study is to evaluate the safety of ExAblate Transcranial MRgFUS as a tool for creating bilateral or unilateral lesions in the globus pallidus (GPi) in patients with treatment-refractory secondary dystonia due to dyskinetic cerebral palsy

Eligibility
Participation Requirements
Sex: All
Minimum Age: 8
Maximum Age: 22
Healthy Volunteers: f
View:

• The treating physician has chosen GPi-DBS or pallidotomy for the treatment of the secondary dystonia caused by cerebral palsy in this patient

• Patient and/or legal representative, if the patient is underaged or not capable to give consent himself, have chosen pallidotomy as treatment

• The consent to participate in the trial of the underaged patient, if he is capable to understand the study requirements, is required

• Age at enrolment 8-22 years

• Diagnosis of secondary dystonia due to cerebral palsy caused by perinatal hypoxic injury

• Anti-dystonic pharmacotherapy insufficient

• Stable anti-dystonic medication over the last 30 days

• Globus pallidus internus (pars posterior) and thalamus (motor part) intact on MRI (not older than 2 years - if possible)

• No fixed severe skeletal deformations with loss of function, which need immediate orthopaedic surgical intervention

• Sufficient compliance of the patient or the legal representative if the patient is underaged or not capable to give consent himself to take part in the study

• Informed consent to take part in the study from patient and/or legal representative if the patient is underaged or not capable to give consent himself

• Patient and/or legal representative if the patient is underaged or not capable to give consent himself, understands the study requirements and the treatment procedures and provides written informed consent before any study-specific tests or procedures are performed

Locations
United States
Washington, D.c.
Children's National Hospital
RECRUITING
Washington D.c.
Contact Information
Primary
Chima Oluigbo, MD
coluigbo@childrensnational.org
2024763531
Backup
Saige Teti
sateti@childrensnational.org
2024763755
Time Frame
Start Date: 2024-01-26
Estimated Completion Date: 2025-08
Participants
Target number of participants: 10
Treatments
Experimental: Focused Ultrasound Pallidotomy
Pediatric and young adult patients between ages of 8 and 22 years with pharmaco-resistant secondary dystonia due to dyskinetic cerebral palsy who have Focused Ultrasound Pallidotomy
Sponsors
Leads: Children's National Research Institute

This content was sourced from clinicaltrials.gov