Prospective Clinical Assessment Study in Children With Hypochondroplasia: ACCEL
Status: Recruiting
Location: See all (25) locations...
Study Type: Observational
SUMMARY
This is a long-term, multicenter, non-interventional study of children ages 2.5 to \<17 years with hypochondroplasia (HCH).
Eligibility
Participation Requirements
Sex: All
Minimum Age: 2
Maximum Age: 16
Healthy Volunteers: f
View:
• Signed informed consent.
• Aged 2.5 to \<17 years at study entry.
• Diagnosis of HCH documented clinically by the presence of disproportionate short stature and confirmed with a molecular test.
• Participants are ambulatory and able to stand without assistance.
• Study participants and parent(s), guardian(s), or caregiver(s) are willing and able to comply with study visits and study procedures.
Locations
United States
California
UCSF Benioff Children's Hospital
RECRUITING
Oakland
Colorado
Childrens Hospital Colorado
RECRUITING
Aurora
Washington, D.c.
Children's National Hospital
RECRUITING
Washington D.c.
Maryland
Johns Hopkins School of Medicine
RECRUITING
Baltimore
Missouri
University of Missouri
RECRUITING
Columbia
Ohio
Cincinnati Children's Hospital Medical Center
RECRUITING
Cincinnati
Tennessee
Vanderbilt University Medical Center
RECRUITING
Nashville
Wisconsin
University of Wisconsin Madison - Waisman Center Bone Dysplasia Clinic
RECRUITING
Madison
Other Locations
Australia
Murdoch Children's Research Institute
RECRUITING
Parkville
Canada
London Health Sciences Centre - Children's Hospital of Western Ontario
RECRUITING
London
Université de Montréal - Centre Hospitalier Universitaire Sainte-Justine
RECRUITING
Montreal
Children's Hospital of Eastern Ontario Research Institute
RECRUITING
Ottawa
France
Hôpital Femme Mère Enfant HCL
RECRUITING
Bron
Hôpital Necker-Enfants Malades
RECRUITING
Paris
Centre Hospitalier Universitaire (CHU) de Toulouse - Hôpital des Enfants
RECRUITING
Toulouse
Norway
Haukeland University Hospital
RECRUITING
Bergen
Paediatric Clinical Research Unit at Oslo University Hospital
RECRUITING
Oslo
Portugal
Hospital Pediátrico de Coimbra
RECRUITING
Coimbra
Singapore
KK Women's and Children's Hospital
RECRUITING
Singapore
Spain
Hospital Vithas San Jose
RECRUITING
Vitoria-gasteiz
Sweden
Astrid Lindgren Children's Hospital
RECRUITING
Solna
United Kingdom
Glasgow Clinical Research Facility, Queen Elizabeth University Hospital
RECRUITING
Glasgow
The Portland Hospital for Women and Children
RECRUITING
London
Manchester University
RECRUITING
Manchester
Sheffield Children's NHS Foundation Trust
RECRUITING
Sheffield
Contact Information
Primary
QED Therapeutics, Inc
medinfo@qedtx.com
1-877-280-5655
Time Frame
Start Date: 2024-06-05
Estimated Completion Date: 2026-10
Participants
Target number of participants: 150
Related Therapeutic Areas
Sponsors
Leads: QED Therapeutics, a BridgeBio company