A Phase II, Open Label, Multi-center Trial to Determine the Efficacy and Safety of Tisagenlecleucel Re-infusion in Pediatric and Adolescent Young Adult (AYA) Patients With Acute Lymphoblastic Leukemia Experiencing Loss of B Cell Aplasia

Who is this study for? Child to young adult CD19-Positive Acute Lymphoblastic Leukemia
What treatments are being studied? Tisagenlecleucel
Status: Terminated
Location: See all (4) locations...
Intervention Type: Biological
Study Type: Interventional
Study Phase: Phase 2
SUMMARY

This was a multi-center Phase II study investigating the efficacy and safety of reinfusion of tisagenlecleucel in pediatric and young adult patients with acute lymphoblastic leukemia (ALL) who were treated with tisagenlecleucel and experience B cell recovery.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 2
Maximum Age: 25
Healthy Volunteers: f
View:

• Signed informed consent must be obtained prior to participation in the study

• Must have an additional dose of unexpired, commercial tisagenlecleucel available and prescribed by a physician in the course of medical practice

• Age up to and including 25 years

• Patients must have CD-19+ Leukemia

• Patients who were previously treated with tisagenlecleucel and present with evidence of B-cell recovery as defined by: Peripheral blood (PB) absolute B lymphocyte count ≥ 50/µL, OR PB B lymphocyte ≥ 10% of the total lymphocytes

Locations
United States
California
Childrens Hospital Los Angeles Divisionof Hematology/Oncology
Los Angeles
Illinois
Ann and Robert H Lurie Childrens Hospital of Chicago
Chicago
Missouri
Children s Mercy Hospital
Kansas City
Texas
UT Southwestern Medical Center
Dallas
Time Frame
Start Date: 2020-10-19
Completion Date: 2021-10-19
Participants
Target number of participants: 5
Treatments
Experimental: Tisagenlecleucel
Tisagenlecleucel Cell Dispersion for Infusion given once during the study.~The approved dose range for tisagenlecleucel is: 0.2 to 5.0×106 CAR positive viable T cells / kg for patients' ≤ 50 kg body weight or 0.1 to 2.5×108 CAR-positive viable T cells for patients \> 50 kg body weight.
Sponsors
Leads: Novartis Pharmaceuticals

This content was sourced from clinicaltrials.gov