A Phase 1 Randomized, Double-blind, Placebo-controlled, Multicenter, Ascending Dose, Safety and PK/PD Study of SHP655 (rADAMTS13) in Sickle Cell Disease at Baseline Health

Who is this study for? Patients with baseline health sickle cell disease and sickle cell disease with acute vaso-occlusive crisis
What treatments are being studied? SHP655
Status: Completed
Location: See all (14) locations...
Intervention Type: Other, Drug
Study Type: Interventional
Study Phase: Phase 1
SUMMARY

TAK-755 (previously known as SHP655) is a medicine used to treat sickle cell disease (SCD). The main aim of the study is to measure the safety and tolerability of TAK-755 in SCD participants. Study participants will receive TAK-755 or placebo on Day 1. Their SCD will be treated by their doctor according to their doctor's usual clinical practice. During the study, participants will be asked to follow-up on 13 days following SHP655 or placebo administration for safety assessment. Maximum duration of participation is expected to be about 2 months.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 18
Maximum Age: 65
Healthy Volunteers: f
View:

• Age 18 to 65 years at the time of signing the informed consent.

• An understanding, ability, and willingness to fully comply with study procedures and requirements.

• Ability to voluntarily provide written, signed, and dated (personally or via a legally authorized representative) informed consent to participate in the study.

• Male or female with a documented history of HbSS or HbSβo thalassemia (based on clinical record of genetic, electrophoresis, or high-performance liquid chromatography testing).

• Participant currently taking hydroxyurea must be on a stable dosing for 3 months at screening.

Locations
United States
Alabama
University of Alabama at Birmingham
Birmingham
Arkansas
Arkansas Children's Hospital
Little Rock
Colorado
University of Colorado Sickle Cell Treatment and Research Center
Aurora
Sickle Cell Center
Denver
Illinois
University of Illinois
Chicago
Louisiana
Ochsner Health System
New Orleans
Maryland
Johns Hopkins University School Of Medicine
Baltimore
North Carolina
Levine Cancer Institute
Charlotte
Duke University Medical Center
Durham
East Carolina University
Greenville
Ohio
Ohio State University Medical Center
Columbus
South Carolina
Medical University of South Carolina (MUSC)
Charleston
Tennessee
University of Tennessee -- Memphis
Memphis
Virginia
VCU Health - Research Parent
Richmond
Time Frame
Start Date: 2019-10-21
Completion Date: 2022-10-26
Participants
Target number of participants: 19
Treatments
Experimental: TAK-755
Participants with SCD at their baseline health will receive a single intravenous (IV) infusion at one of the 3 dose levels of 40, 80 and 160 International units per kilogram (IU/kg) in a dose escalation manner.
Placebo_comparator: Placebo
Participants with SCD at their baseline health will receive placebo matched to TAK-755 of the 3 dose levels of 40 IU/kg, 80 IU/kg, and 160 IU/kg as single IV infusion.
Sponsors
Collaborators: Takeda Development Center Americas, Inc.
Leads: Shire

This content was sourced from clinicaltrials.gov

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