A Phase 3, Pivotal, Open-label, Multicenter Study to Assess the Efficacy and Safety of Sutimlimab in Patients With Primary Cold Agglutinin Disease Who Have a Recent History of Blood Transfusion

Who is this study for? Adult patients with Cold Agglutinin Disease
What treatments are being studied? Sutimlimab
Status: Completed
Location: See all (49) locations...
Intervention Type: Drug
Study Type: Interventional
Study Phase: Phase 3
SUMMARY

The purpose of Part A was to determine whether sutimlimab administration resulted in a greater than or equal to (\>=) 2 grams per deciliter (g/dL) increase in hemoglobin (Hgb) levels or increased Hgb to \>= 12 g/dL and obviated the need for blood transfusion during treatment in participants with primary cold agglutinin disease (CAD) who had a recent history of blood transfusion. The purpose of Part B was to evaluate the long-term safety and tolerability of sutimlimab in participants with CAD.

Eligibility
Participation Requirements
Sex: All
Minimum Age: 18
Healthy Volunteers: f
View:

• Body weight of \>= 39 kg at screening.

• Confirmed diagnosis of primary CAD based on the following criteria: a) Chronic hemolysis; b) Polyspecific direct antiglobulin test (DAT) positive; c) Monospecific DAT strongly positive for C3d; d) Cold agglutinin titer \>= 64 at 4 degree celsius; e) Immunoglobulin G (IgG) DAT less than or equal to (\<=) 1+, and f) No overt malignant disease.

• History of at least one documented blood transfusion within 6 months of enrollment.

• Hemoglobin level \<= 10.0 g/dL.

• Bilirubin level above the normal reference range, including participants with Gilbert's Syndrome.

Locations
United States
Arizona
Arizona Oncology Associates PC
Tucson
California
USC/Keck School of Medicine
Los Angeles
The Oncology Institute of Hope and Innovation
Whittier
Washington, D.c.
Georgetown University Medical Center
Georgetown
Massachusetts
Brigham and Women's Hospital
Boston
Massachusetts General Hospital
Boston
North Carolina
East Carolina University
Greenville
New York
Montefiore Medical Center
New York
New York Medical College at Westchester Medical Center
Valhalla
Ohio
Cleveland Clinic
Cleveland
Pennsylvania
Hospital of the University of Pennsylvania
Philadelphia
University of Pittsburgh Medical Center
Pittsburgh
Wisconsin
UW Hospitals and Clinics
Madison
Other Locations
Australia
Ballarat Oncology & Haematology
Ballarat
USC Health Clinics
Buderim
Monash Medical Centre
Clayton
Austria
Medical University of Vienna
Vienna
Belgium
ZNA Stuivenberg
Antwerpen
Centre Hospitalier Jolimont
La Louvière
University Hospitals Leuven
Leuven
Canada
University of Alberta
Edmonton
McGill University Health Center
Montréal
St. Michael's Hospital
Toronto
France
CHU de Caen
Caen
Centre Hospitalier Henri Mondor
Créteil
Centre Hospitalier Lyon Sud
Lyon
Germany
Gemeinschaftspraxis Hämatologie-Onkologie
Dresden
Universitätsklinikum Essen
Essen
Univ Ulm, Inst Klin. Transfusions. Immungen
Ulm
Israel
Hadassah Medical Center
Jerusalem
Laniado Hospital
Netanya
Tel Aviv Sourasky Medical Center
Tel Aviv
Italy
A. O. Spedali Civili di Brescia
Brescia
Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico
Milan
U.O.C. Ematologia- Policlinico A. Gemelli
Rome
U.O.C. Ematologia Ospedale San Bortolo
Vicenza
Japan
Saitama Medical University Hospital
Iruma-gun
Tokai University Hospital
Isehara
Juntendo University Nerima Hospital
Tokyo
Netherlands
Academisch Medisch Centrum
Amsterdam
Norway
Haukeland University Hospital
Bergen
Oslo University Hospital
Oslo
St Olavs Hospital, Avdeling for blodsykdommer
Trondheim
Spain
Hospital Clinci i Provincial de Barcelona
Barcelona
Hospital Universitario Puerta de Hierro
Majadahonda
Hospital Universitario Virgen del Rocio
Sevilla
Hospital Universitario Dr. Peset
Valencia
United Kingdom
St James Hospital, Leeds
Leeds
University College London
London
Time Frame
Start Date: 2018-03-05
Completion Date: 2021-10-05
Participants
Target number of participants: 24
Treatments
Experimental: BIVV009
Participants with primary CAD who had a recent history of transfusion (defined as at least 1 transfusion during the last 6 months prior to screening) received an intravenous (IV) infusion of BIVV009 6.5 grams (g) (if body weight was less than \[\<\] 75 kilograms \[kg\]) or BIVV009 7.5 g (if body weight was greater than or equal to \[\>=\] 75 kg) on Day 0 and Day 7 and every 14 days thereafter in Part A up to Week 25. Participants who completed Part A per protocol through the end of treatment visit (Week 26) could continue to receive BIVV009 in Part B, every 2 weeks starting at Week 27 for up to an additional 149 weeks. All participants who completed Part A elected to continue in Part B.
Sponsors
Leads: Bioverativ, a Sanofi company

This content was sourced from clinicaltrials.gov